The New England Journal of Medicine -- September 18, 1997 -- Volume 337,

Number 12

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[SOUNDING BOARD]

Unethical Trials of Interventions to Reduce Perinatal Transmission of the

Human Immunodeficiency Virus in Developing Countries

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Defining Placebo as the Standard of Care in Developing Countries

Some officials and researchers have defended the use of

placebo-controlled studies in developing countries by arguing

that the subjects are treated at least according to the standard

of care in these countries, which consists of unproven regimens

or no treatment at all. This assertion reveals a fundamental

misunderstanding of the concept of the standard of care. In

developing countries, the standard of care (in this case, not

providing zidovudine to HIV-positive pregnant women) is not based

on a consideration of alternative treatments or previous clinical

data, but is instead an economically determined policy of

governments that cannot afford the prices set by drug companies.

We agree with the Council for International Organizations of

Medical Sciences that researchers working in developing countries

have an ethical responsibility to provide treatment that conforms

to the standard of care in the sponsoring country, when possible.

(9) An exception would be a standard of care that required an

exorbitant expenditure, such as the cost of building a coronary

care unit. Since zidovudine is usually made available free of

charge by the manufacturer for use in clinical trials, excessive

cost is not a factor in this case. Acceptance of a standard of

care that does not conform to the standard in the sponsoring

country results in a double standard in research. Such a double

standard, which permits research designs that are unacceptable in

the sponsoring country, creates an incentive to use as research

subjects those with the least access to health care.

What are the potential implications of accepting such a double

standard? Researchers might inject live malaria parasites into

HIV-positive subjects in China in order to study the effect on

the progression of HIV infection, even though the study protocol

had been rejected in the United States and Mexico. Or researchers

might randomly assign malnourished San (bushmen) to receive

vitamin-fortified or standard bread. One might also justify

trials of HIV vaccines in which the subjects were not provided

with condoms or state-of-the-art counseling about safe sex by

arguing that they are not customarily provided in the developing

countries in question. These are not simply hypothetical

worst-case scenarios; the first two studies have already been

performed, (22,23) and the third has been proposed and

criticized. (24)

Annas and Grodin recently commented on the characterization and

justification of placebos as a standard of care: "'Nothing' is a

description of what happens; 'standard of care' is a normative

standard of effective medical treatment, whether or not it is

provided to a particular community." (25)

 

References

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Return to: Introduction

2. Sperling RS, Shapiro DE, Coombs RW, et al. Maternal viral

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1996;335:1621-9.

Return to: Introduction

3. Recommendations of the U.S. Public Health Service Task Force

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1994;43(RR-11):1-20.

Return to: Introduction

4. Fiscus SA, Adimora AA, Schoenbach VJ, et al. Perinatal HIV

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Return to: Introduction

5. Cooper E, Diaz C, Pitt J, et al. Impact of ACTG 076: use of

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Return to: Introduction

6. Simonds RJ, Nesheim S, Matheson P, et al. Declining mother to

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Return to: Introduction

7. Scarlatti G. Paediatric HIV infection. Lancet 1996;348:863-8.

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8. Recommendations from the meeting on mother-to-infant

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Return to: Introduction

9. World Health Organization. International ethical guidelines

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for International Organizations of Medical Sciences, 1993.

Return to: Introduction | Defining Placebo as the Standard of

Care in Developing Countries

10. 45 CFR 46.111(a)(1).

Return to: Introduction

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Claiming They Are More Rapid

12. Brennan TA. Letter to Gilbert Meier, NIH Division of Research

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Return to: Introduction

13. Lallemant M, Vithayasai V. A short ZDV course to prevent

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Return to: Asking the Wrong Research Question

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Return to: Inadequate Analysis of Data from ACTG 076 and Other

Sources

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Sources

17. Questions and answers on the UNAIDS sponsored trials for the

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Sources

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Johns Hopkins University, May 6, 1997.

Return to: Inadequate Analysis of Data from ACTG 076 and Other

Sources

19. Wiktor SZ, Ehounou E. A randomized placebo-controlled

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Sources

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Sources

21. Freedman B. Equipoise and the ethics of clinical research. N

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Return to: Inadequate Analysis of Data from ACTG 076 and Other

Sources

22. Heimlich HJ, Chen XP, Xiao BQ, et al. CD4 response in

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7-12, 1996. abstract.

Return to: Defining Placebo as the Standard of Care in Developing

Countries

23. Bishop WB, Laubscher I, Labadarios D, Rehder P, Louw ME,

Fellingham SA. Effect of vitamin-enriched bread on the vitamin

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trial. S Afr Med J 1996;86:Suppl:458-62.

Return to: Defining Placebo as the Standard of Care in Developing

Countries

24. Lurie P, Bishaw M, Chesney MA, et al. Ethical, behavioral,

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JAMA 1994;271:295-301.

Return to: Defining Placebo as the Standard of Care in Developing

Countries

25. Annas G, Grodin M. An apology is not enough. Boston Globe.

May 18, 1997:C1-C2.

Return to: Defining Placebo as the Standard of Care in Developing

Countries

26. Freedman B, Weijer C, Glass KC. Placebo orthodoxy in clinical

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Return to: Justifying Placebo-Controlled Trials by Claiming They

Are More Rapid

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12, 1996.

Return to: Toward a Single International Standard of Ethical

Research

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Return to: Toward a Single International Standard of Ethical

Research

Copyright © 1997 by the Massachusetts Medical Society